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P281: JOURNEY: A natural history study of limb-girdle muscular dystrophies R3–R5, baseline characteristics of study cohort by Linda P. Lowes, Carlos Ortez Gonzalez, Kristl Claeys, Chamindra Laverty, Andrea Gangfuss, Crystal Proud, Jordi Diaz Manera, Meredith James, Lindsay Alfano, Herb Stevenson, Lixi Yu, André Mueller-York, Giacomo Comi
Published 2025-01-01Get full text
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Myostatin Levels in SMA Following Disease‐Modifying Treatments: A Multi‐Center Study by Fiorella Piemonte, Sara Petrillo, Anna Capasso, Giorgia Coratti, Adele D'Amico, Michela Catteruccia, Maria Carmela Pera, Concetta Palermo, Marika Pane, Emanuela Abiusi, Gianpaolo Cicala, Marianna Villa, Chiara Bravetti, Chiara Arpaia, Agnese Novelli, Salvatore Falqui, Stefania Fiori, Giulia Napoli, Silvia Baroni, Francesco Danilo Tiziano, Enrico Bertini, Giacomo Comi, Stefania Corti, Eugenio Mercuri
Published 2025-07-01Get full text
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