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circARHGAP10 as a candidate biomarker and therapeutic target in myotonic dystrophy type 1 by Denisa Baci, Spyros Tastsoglou, Claudia Provenzano, Alessandra Perfetti, Mariapaola Izzo, Mario Lisanti, Svetlana Frolova, Christine Voellenkle, Anna Sofia Tascini, Rosanna Cardani, Beatrice Cardinali, Giovanni Meola, Germana Falcone, Fabio Martelli
Published 2025-09-01Get full text
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Muscle‐specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1 by Mariapaola Izzo, Jonathan Battistini, Elisabetta Golini, Christine Voellenkle, Claudia Provenzano, Tiziana Orsini, Georgios Strimpakos, Ferdinando Scavizzi, Marcello Raspa, Denisa Baci, Svetlana Frolova, Spyros Tastsoglou, Germana Zaccagnini, Jose Manuel Garcia‐Manteiga, Genevieve Gourdon, Silvia Mandillo, Beatrice Cardinali, Fabio Martelli, Germana Falcone
Published 2025-02-01Get full text
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