The GATA1-HS2 enhancer allows persistent and position-independent expression of a β-globin transgene. by Annarita Miccio, Valentina Poletti, Valentina Poletti, Francesca Tiboni, Claudia Rossi, Antonella Antonelli, Fulvio Mavilio, Giuliana Ferrari

Get full text

Transcription factor binding sites are genetic determinants of retroviral integration in the human genome. by Barbara Felice, Claudia Cattoglio, Davide Cittaro, Anna Testa, Annarita Miccio, Giuliana Ferrari, Lucilla Luzi, Alessandra Recchia, Fulvio Mavilio

Get full text

Muscle‐directed gene therapy corrects Pompe disease and uncovers species‐specific GAA immunogenicity by Michelle Eggers, Charles H Vannoy, Jianyong Huang, Pravinkumar Purushothaman, Jacqueline Brassard, Carlos Fonck, Hui Meng, Mariah J Prom, Michael W Lawlor, Justine Cunningham, Chanchal Sadhu, Fulvio Mavilio

Get full text

High-definition mapping of retroviral integration sites defines the fate of allogeneic T cells after donor lymphocyte infusion. by Claudia Cattoglio, Giulietta Maruggi, Cynthia Bartholomae, Nirav Malani, Danilo Pellin, Fabienne Cocchiarella, Zulma Magnani, Fabio Ciceri, Alessandro Ambrosi, Christof von Kalle, Frederic D Bushman, Chiara Bonini, Manfred Schmidt, Fulvio Mavilio, Alessandra Recchia

Get full text

A single epidermal stem cell strategy for safe ex vivo gene therapy by Stéphanie Droz‐Georget Lathion, Ariane Rochat, Graham Knott, Alessandra Recchia, Danielle Martinet, Sara Benmohammed, Nicolas Grasset, Andrea Zaffalon, Nathalie Besuchet Schmutz, Emmanuelle Savioz‐Dayer, Jacques Samuel Beckmann, Jacques Rougemont, Fulvio Mavilio, Yann Barrandon

Get full text