Antisense oligonucleotide therapy for patients with Friedreich’s ataxia carrying the c.165+5G>C splicing mutation by Pouiré Yameogo, Selina Aguilar, Thazha P. Prakash, Frank Rigo, David R. Lynch, Jill S. Napierala, Marek Napierala

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Employing splice-switching oligonucleotides and AAVrh74.U7 snRNA to target insulin receptor splicing and cancer hallmarks in osteosarcoma by Safiya Khurshid, Akila S. Venkataramany, Matias Montes, John F. Kipp, Ryan D. Roberts, Nicolas Wein, Frank Rigo, Pin-Yi Wang, Timothy P. Cripe, Dawn S. Chandler

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The differential impact of HNRNPA1 isoforms on gene expression and their relevance to dsRNA-mediated innate immune response by Jade-Emmanuelle Deshaies, Valérie Triassi, Andréanne Lacombe, Myriam Gagné, Karen Ling, Asmita Ghosh, Marjorie Labrecque, Frank Rigo, Paymaan Jafar-nejad, Martine Tétreault, Christine Vande Velde

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Therapeutic correction of ApoER2 splicing in Alzheimer's disease mice using antisense oligonucleotides by Anthony J Hinrich, Francine M Jodelka, Jennifer L Chang, Daniella Brutman, Angela M Bruno, Clark A Briggs, Bryan D James, Grace E Stutzmann, David A Bennett, Steven A Miller, Frank Rigo, Robert A Marr, Michelle L Hastings

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