Muscle‐specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1 by Mariapaola Izzo, Jonathan Battistini, Elisabetta Golini, Christine Voellenkle, Claudia Provenzano, Tiziana Orsini, Georgios Strimpakos, Ferdinando Scavizzi, Marcello Raspa, Denisa Baci, Svetlana Frolova, Spyros Tastsoglou, Germana Zaccagnini, Jose Manuel Garcia‐Manteiga, Genevieve Gourdon, Silvia Mandillo, Beatrice Cardinali, Fabio Martelli, Germana Falcone

Get full text

Estrogen rescues muscle regeneration impaired by DUX4 in a humanized xenograft mouse model by Silvia Maiullari, Giada Mele, Patrizia Calandra, Giorgia di Blasio, Sonia Valentini, Alessio Torcinaro, Isabella Manni, Emanuela Teveroni, Fabio Mancino, Luca Proietti, Fabio Maiullari, Maria Pesavento, Ludovica Giorgini, Sabrina Putti, Roberto Rizzi, Sara Bortolani, Ferdinando Scavizzi, Marcello Raspa, Enzo Ricci, Giulia Piaggio, Cesare Gargioli, Alfredo Pontecorvi, Siro Luvisetto, Massimiliano Mazzone, Giancarlo Deidda, Fabiola Moretti

Get full text