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A one-base therapeutic insertion in the HBG2 distal promoter reactivates γ-globin expression by Xiuqin Bao, Yuanyi Gao, Xiaoyi Chen, Zhongju Wang, Xiaoqin Feng, Liren Wang, Jing Du, Yuhua Ye, Feijing Chen, Li Du, Aihua Yin, Xiangmin Xu
Published 2025-03-01Get full text
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