Disease rescue and increased lifespan in a model of cardiomyopathy and muscular dystrophy by combined AAV treatments. by Carmen Vitiello, Stefania Faraso, Nicolina Cristina Sorrentino, Giovanni Di Salvo, Edoardo Nusco, Gerardo Nigro, Luisa Cutillo, Raffaele Calabrò, Alberto Auricchio, Vincenzo Nigro

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Liver gene therapy with intein‐mediated F8 trans‐splicing corrects mouse haemophilia A by Federica Esposito, Hristiana Lyubenova, Patrizia Tornabene, Stefano Auricchio, Antonella Iuliano, Edoardo Nusco, Simone Merlin, Cristina Olgasi, Giorgia Manni, Marco Gargaro, Francesca Fallarino, Antonia Follenzi, Alberto Auricchio

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Liver‐directed gene therapy for ornithine aminotransferase deficiency by Iolanda Boffa, Elena Polishchuk, Lucia De Stefano, Fabio Dell'Aquila, Edoardo Nusco, Elena Marrocco, Matteo Audano, Silvia Pedretti, Marianna Caterino, Ilaria Bellezza, Margherita Ruoppolo, Nico Mitro, Barbara Cellini, Alberto Auricchio, Nicola Brunetti‐Pierri

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Correction of oxidative stress enhances enzyme replacement therapy in Pompe disease by Antonietta Tarallo, Carla Damiano, Sandra Strollo, Nadia Minopoli, Alessia Indrieri, Elena Polishchuk, Francesca Zappa, Edoardo Nusco, Simona Fecarotta, Caterina Porto, Marcella Coletta, Roberta Iacono, Marco Moracci, Roman Polishchuk, Diego Luis Medina, Paola Imbimbo, Daria Maria Monti, Maria Antonietta De Matteis, Giancarlo Parenti

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Impact of liver fibrosis on AAV-mediated gene transfer to mouse hepatocytes by Rosa Ferriero, Gemma Bruno, Agnese Padula, Simone Pisano, Iolanda Boffa, Marco Gargaro, Teresa Imperatore, Maria Battipaglia, Silvia Vivenzio, Claudia Perna, Edoardo Nusco, Luigi Ferrante, Adrian Westhaus, Maddison Knight, Giorgia Manni, Severo Campione, Evaristo Di Napoli, Elena Polishchuk, Roman Polishchuk, Orlando Paciello, Nicola Brunetti-Pierri, Leszek Lisowski, Francesca Fallarino, Pasquale Piccolo

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TFEB and TFE3 drive kidney cystogenesis and tumorigenesis by Chiara Di Malta, Angela Zampelli, Letizia Granieri, Claudia Vilardo, Rossella De Cegli, Laura Cinque, Edoardo Nusco, Salvatore Pece, Daniela Tosoni, Francesca Sanguedolce, Nicolina Cristina Sorrentino, Maria J Merino, Deborah Nielsen, Ramaprasad Srinivasan, Mark W Ball, Christopher J Ricketts, Cathy D Vocke, Martin Lang, Baktiar Karim, Luisa Lanfrancone, Laura S Schmidt, W Marston Linehan, Andrea Ballabio

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