Showing 1 - 2 results of 2 for search 'EVIDENCE‐RND consortium', query time: 0.01s Refine Results
  1. 1
    Item performance of the scale for the assessment and rating of ataxia in rare and ultra‐rare genetic ataxias

    Item performance of the scale for the assessment and rating of ataxia in rare and ultra‐rare genetic ataxias by Alzahra Hamdan, Andrew C. Hooker, Xiaomei Chen, Andreas Traschütz, Rebecca Schüle, ARCA Study Group, EVIDENCE‐RND consortium, Matthis Synofzik, Mats O. Karlsson

    Published 2024-08-01
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  2. 2
    Comparing randomized trial designs to estimate treatment effect in rare diseases with longitudinal models: a simulation study showcased by Autosomal Recessive Cerebellar Ataxias using the SARA score

    Comparing randomized trial designs to estimate treatment effect in rare diseases with longitudinal models: a simulation study showcased by Autosomal Recessive Cerebellar Ataxias us... by Niels Hendrickx, France Mentré, Alzahra Hamdan, Mats O. Karlsson, Andrew C. Hooker, Andreas Traschütz, Cynthia Gagnon, Rebecca Schüle, Matthis Synofzik, Emmanuelle Comets, ARCA Study Group, EVIDENCE-RND consortium

    Published 2025-07-01
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