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Targeted gene editing and near-universal cDNA insertion of CYBA and CYBB as a treatment for chronic granulomatous disease by Jonas Holst Wolff, Thomas Wisbech Skov, Didde Haslund, Sofie Rahbek Dorset, Anne Louise S. Revenfeld, Clotilde Aussel, Sofie E. Jørgensen, Mette Holm, Martin K. Thomsen, Sandra Ammann, Toni Cathomen, Trine H. Mogensen, Bjarne Kuno Møller, Rasmus O. Bak, Jacob Giehm Mikkelsen
Published 2025-08-01Get full text
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