In vivo base editing of Angptl3 via lipid nanoparticles to treat cardiovascular disease by Jennifer Khirallah, Hanan Bloomer, Douglas Wich, Changfeng Huang, J. Noah Workman, Yamin Li, Gregory A. Newby, David R. Liu, Qiaobing Xu

Get full text

In vivo prime editing rescues photoreceptor degeneration in nonsense mutant retinitis pigmentosa by Yidian Fu, Xiaoyu He, Liang Ma, Xin D. Gao, Pengpeng Liu, Hanhan Shi, Peiwei Chai, Shengfang Ge, Renbing Jia, David R. Liu, Xianqun Fan, Zhi Yang

Get full text

Multiplex base editing to protect from CD33 directed drugs for immune and gene therapy by Florence Borot, Olivier Humbert, Jeffrey T. Ehmsen, Emily Fields, Sajeev Kohli, Stefan Radtke, Kyle Swing, Dnyanada Pande, Mark R. Enstrom, George S. Laszlo, Thiyagaraj Mayuranathan, Abdullah Mahmood Ali, Mitchell J. Weiss, Jonathan S. Yen, Gregory A. Newby, Roland B. Walter, David R. Liu, Siddhartha Mukherjee, Hans-Peter Kiem

Get full text

GFP-on mouse model for interrogation of in vivo gene editing by Carla Dib, Jack A. Queenan, Leah Swartzrock, Hana Willner, Morgane Denis, Nouraiz Ahmed, Fareha Moulana Zada, Beltran Borges, Carsten T. Charlesworth, Tony Lum, Bradley P. Yates, Caleb Y. Kwon, Augustino V. Scorzo, Scott C. Davis, Jessie R. Davis, Ran He, Jun Xie, Guangping Gao, Tippi C. MacKenzie, David R. Liu, Gregory A. Newby, Agnieszka D. Czechowicz

Get full text