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Empagliflozin Repurposing for Lafora Disease: A Pilot Clinical Trial and Preclinical Investigation of Novel Therapeutic Targets by Giuseppe d’Orsi, Antonella Liantonio, Paola Imbrici, Nicola Gambacorta, Giorgia Dinoi, Cosimo Damiano Altomare, DEFEAT-LD Study Group, Massimo Carella
Published 2025-05-01Get full text
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Generation of a human induced pluripotent stem cell line (CIBIOi007-A) from a Lafora disease patient by Gabriele Trentini, Giulia Cazzanelli, Marina Cardano, Orazio Palumbo, Mario Benvenuto, Pietro Palumbo, Francesca Agriesti, Claudia Piccoli, Luciano Conti, DEFEAT-LD Study Group, Massimo Carella, Graziano Lolli, Giuseppe d’Orsi
Published 2025-09-01Get full text
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Clinical course and management challenges in Lafora disease: a narrative analysis in an Apulian cohort by Giuseppe d’Orsi, Maria Teresa Di Claudio, Antonella Liantonio, Paola Imbrici, Cosimo Damiano Altomare, Orazio Palumbo, Pietro Palumbo, Mario Benvenuto, Nicola Gambacorta, Graziano Lolli, DEFEAT-LD study group, Massimo Carella
Published 2025-08-01Get full text
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