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Using muscle homing peptide CyPep10 to deliver phosphorodiamidate morpholino oligomers in the mdx mouse by Anne-Fleur E. Schneider, Christa L. Tanganyika-de Winter, Silvana M.G. Jirka, Xuyu Tan, Emily G. Thompson, Kristen Ha, Anindita Mitra, Stephanie Garcia, Marleen Luimes, Ryan A. Oliver, Vincent Guerlavais, Annemieke Aartsma-Rus
Published 2025-09-01Get full text
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Splicing correction by peptide-conjugated morpholinos as a novel treatment for late-onset Pompe disease by Ryan A. Oliver, Meghan E. Ahern, Perla G. Castaneda, Tushare Jinadasa, Anirban Bardhan, Kathy Y. Morgan, Kristin Ha, Kailash Adhikari, Nino Jungels, Noa Liberman, Anindita Mitra, Christopher D. Greer, Alec M. Wright, Emily G. Thompson, Stephanie Garcia, Elena Copson, Senkara Allu, Xuyu Tan, Alex J. Callahan, Bao Zhong Cai, Vincent Guerlavais, Kevin J. Kim, Annika B. Malmberg
Published 2025-06-01Get full text
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