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Biomarker Evolution in Pediatric SMA: Insights from CSF pNF-H Dynamics and SMN2 Copy Number During Nusinersen Therapy by Mihaela Badina, Gabriel Cristian Bejan, Andrada Mirea, Corina Sporea, Madalina Cristina Leanca, Georgiana Nicolae, Ioana Elena Cioca, Maria Veronica Morcov, Angelo Pellegrini, Elena-Nicoleta Bordea
Published 2025-03-01Get full text
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New Perspectives of Underlying Cardiomyopathy in Pediatric SMA Patients—An Age Matched Control Study by Georgiana Nicolae, Andrei Capitanescu, Madalina Cristina Leanca, Elena Neagu, Daniela Vasile, Cristina Filip, Eliza Cinteza, Amelia Aria, Bianka Maria Pavlov, Gabriela Uscoiu, Cristiana Ioana Raita, Andrada Mirea
Published 2025-07-01Get full text
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